NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)

Publikation: Bidrag til tidsskriftKonferenceabstrakt i tidsskriftForskningfagfællebedømt

Standard

NEO1/NEO-EXT studies : Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD). / Schoser, B.; Barohn, R.; Byrne, B.; Goker-Alpan, O.; Kishnani, P.; Ladha, S.; Laforet, P.; Mengel, E.; Pena, L.; Sacconi, S.; Straub, V.; Trivedi, J.; Van Damme, P.; van der Ploeg, A.; Vissing, J.; Young, P.; Haack, K.; Ivanina, I.; Wang, Y.; Dimachkie, M.

I: Neuromuscular Disorders, Bind 30, 10.2020, s. S49.

Publikation: Bidrag til tidsskriftKonferenceabstrakt i tidsskriftForskningfagfællebedømt

Harvard

Schoser, B, Barohn, R, Byrne, B, Goker-Alpan, O, Kishnani, P, Ladha, S, Laforet, P, Mengel, E, Pena, L, Sacconi, S, Straub, V, Trivedi, J, Van Damme, P, van der Ploeg, A, Vissing, J, Young, P, Haack, K, Ivanina, I, Wang, Y & Dimachkie, M 2020, 'NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)', Neuromuscular Disorders, bind 30, s. S49. https://doi.org/10.1016/j.nmd.2020.08.012

APA

Schoser, B., Barohn, R., Byrne, B., Goker-Alpan, O., Kishnani, P., Ladha, S., Laforet, P., Mengel, E., Pena, L., Sacconi, S., Straub, V., Trivedi, J., Van Damme, P., van der Ploeg, A., Vissing, J., Young, P., Haack, K., Ivanina, I., Wang, Y., & Dimachkie, M. (2020). NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD). Neuromuscular Disorders, 30, S49. https://doi.org/10.1016/j.nmd.2020.08.012

Vancouver

Schoser B, Barohn R, Byrne B, Goker-Alpan O, Kishnani P, Ladha S o.a. NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD). Neuromuscular Disorders. 2020 okt.;30:S49. https://doi.org/10.1016/j.nmd.2020.08.012

Author

Schoser, B. ; Barohn, R. ; Byrne, B. ; Goker-Alpan, O. ; Kishnani, P. ; Ladha, S. ; Laforet, P. ; Mengel, E. ; Pena, L. ; Sacconi, S. ; Straub, V. ; Trivedi, J. ; Van Damme, P. ; van der Ploeg, A. ; Vissing, J. ; Young, P. ; Haack, K. ; Ivanina, I. ; Wang, Y. ; Dimachkie, M. / NEO1/NEO-EXT studies : Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD). I: Neuromuscular Disorders. 2020 ; Bind 30. s. S49.

Bibtex

@article{5bc8fb93d89240709c92222a55c077e0,
title = "NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)",
author = "B. Schoser and R. Barohn and B. Byrne and O. Goker-Alpan and P. Kishnani and S. Ladha and P. Laforet and E. Mengel and L. Pena and S. Sacconi and V. Straub and J. Trivedi and {Van Damme}, P. and {van der Ploeg}, A. and J. Vissing and P. Young and K. Haack and I. Ivanina and Y. Wang and M. Dimachkie",
year = "2020",
month = oct,
doi = "10.1016/j.nmd.2020.08.012",
language = "English",
volume = "30",
pages = "S49",
journal = "Journal of Neuromuscular Diseases",
issn = "0960-8966",
publisher = "Elsevier",
note = "25th International Congress of the World-Muscle-Society (WMS) ; Conference date: 28-09-2020 Through 02-10-2020",

}

RIS

TY - ABST

T1 - NEO1/NEO-EXT studies

T2 - 25th International Congress of the World-Muscle-Society (WMS)

AU - Schoser, B.

AU - Barohn, R.

AU - Byrne, B.

AU - Goker-Alpan, O.

AU - Kishnani, P.

AU - Ladha, S.

AU - Laforet, P.

AU - Mengel, E.

AU - Pena, L.

AU - Sacconi, S.

AU - Straub, V.

AU - Trivedi, J.

AU - Van Damme, P.

AU - van der Ploeg, A.

AU - Vissing, J.

AU - Young, P.

AU - Haack, K.

AU - Ivanina, I.

AU - Wang, Y.

AU - Dimachkie, M.

PY - 2020/10

Y1 - 2020/10

U2 - 10.1016/j.nmd.2020.08.012

DO - 10.1016/j.nmd.2020.08.012

M3 - Conference abstract in journal

VL - 30

SP - S49

JO - Journal of Neuromuscular Diseases

JF - Journal of Neuromuscular Diseases

SN - 0960-8966

Y2 - 28 September 2020 through 2 October 2020

ER -

ID: 269512652