NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)

Publikation: Bidrag til tidsskriftKonferenceabstrakt i tidsskriftForskningfagfællebedømt

  • B. Schoser
  • R. Barohn
  • B. Byrne
  • O. Goker-Alpan
  • P. Kishnani
  • S. Ladha
  • P. Laforet
  • E. Mengel
  • L. Pena
  • S. Sacconi
  • V. Straub
  • J. Trivedi
  • P. Van Damme
  • A. van der Ploeg
  • Vissing, John
  • P. Young
  • K. Haack
  • I. Ivanina
  • Y. Wang
  • M. Dimachkie
OriginalsprogEngelsk
TidsskriftNeuromuscular Disorders
Vol/bind30
Sider (fra-til)S49
Antal sider1
ISSN0960-8966
DOI
StatusUdgivet - okt. 2020
Begivenhed25th International Congress of the World-Muscle-Society (WMS) -
Varighed: 28 sep. 20202 okt. 2020

Konference

Konference25th International Congress of the World-Muscle-Society (WMS)
Periode28/09/202002/10/2020

ID: 269512652