Baseline patient characteristics of followME, a new, patient-centric, prospective, observational Fabry disease registry that evaluates migalastat, ERT, and a natural history cohort

Publikation: Bidrag til tidsskrift › Konferenceabstrakt i tidsskrift › Forskning › fagfællebedømt

  • Gere Sunder-Plassmann
  • Daniel G. Bichet
  • Martynas Davidonis
  • Dominique P. Germain
  • Roberto Giugliani
  • Robert J. Hopkin
  • Ana Jovanovic
  • Ales Linhart
  • Kathleen Nicholls
  • Peter Nordbeck
  • Feldt-Rasmussen, Ulla
  • Jasmine Rutecki
  • Joe Giuliano
  • Nina Skuban
  • Eva Krusinska
  • Juan Politei
OriginalsprogEngelsk
TidsskriftMolecular Genetics and Metabolism
Vol/bind129
Udgave nummer2
Sider (fra-til)S150-S150
Antal sider1
ISSN1096-7192
DOI
StatusUdgivet - 2020
Begivenhed16th Annual Research Meeting of the WORLDSymposium(TM) - Orlando
Varighed: 10 feb. 2020 → 14 feb. 2020

Konference

Konference16th Annual Research Meeting of the WORLDSymposium(TM)
ByOrlando
Periode10/02/2020 → 14/02/2020

ID: 269592262