Bibliografisk note

Funding Information:
The workshop was made possible thanks to the financial support of the European Neuromuscular center (ENMC) and ENMC main sponsors: Association Française contre les Myopathies (France), Deutsche Gesellschaft für Muskelkranke (Germany), Muscular Dystrophy Campaign (UK), Muskelsvindfonden (Denmark), Prinses Beatrix Fonds (The Netherlands), Schweizerische Stiftung für die Erforschung der Muskelkrankheiten (Switzerland), Telethon Foundation (Italy), Spierziekten Nederland (The Netherlands), and Associated Partners: Finnish Neuromuscular Association (Finland), Österreichische Muskelforschung (Austria), SMA Europe and World Duchenne organisation. In addition, we would like to thank the members of the ENMC Company Forum: Sanofi, Roche, Lupin Neuroscience, Amicus Therapeutics, Ionis Pharmaceuticals, Biogen, Novartis, PerkinElmer and Astellas.

Funding Information:
Data presented by Anna Pichiecchio were generated in a project funded by Italian Ministry of Health (RF-2016–02362914).

Funding Information:
This workshop was supported by the European Neuromuscular center (ENMC).

Funding Information:
- Hermien Kan receives research support from Philips Healhtcare and trial support from ImagingDMD. No personal fees are received, all revenues go to the LUMC;