Bibliografisk note

Funding Information:
The workshop was made possible thanks to the financial support of the European Neuromuscular Centre (ENMC) and ENMC main sponsors: Association Française contre les Myopathies (France) , Deutsche Gesellschaft für Muskelkranke (Germany) , Muscular Dystrophy Campaign (UK) , Muskelsvindfonden (Denmark) , Prinses Beatrix Fonds (The Netherlands) , Schweizerische Stiftung für die Erforschung der Muskelkrankheiten (Switzerland) , Telethon Foundation (Italy) , Spierziekten Nederland (The Netherlands) , and Associated members Partners: Finnish Neuromuscular Association (Finland) , Österreichische Muskelforschung (Austria) , SMA Europe and World Duchenne Organisation . In addition, we would like to thank the members of the ENMC Company Forum: Sanofi, Roche, Lupin Neuroscience, Amicus Therapeutics, Ionis Pharmaceuticals, Biogen, Novartis, PerkinElmer and Astellas.